$2.5m medicine is ‘game-changer’ for infants with genetic disorder – BBC News

BBC News published this video item, entitled “$2.5m medicine is ‘game-changer’ for infants with genetic disorder – BBC News” – below is their description.

A baby boy has become one of the first patients to be treated on the UK’s NHS with Zolgensma, the world’s most expensive medicine.

Little Arthur is one of around 40 children are born with the most severe form of Spinal Muscular Atrophy (SMA) every year.

The gene therapy has a list price of about $2.5m and is manufactured by Novartis Gene Therapies.

BBC News YouTube Channel

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About This Source - BBC News

The video item below is a piece of English language content from BBC News. The British Broadcasting Corporation (BBC) is a British public service broadcaster funded by the UK Government, and British license fee payers. Its headquarters are at Broadcasting House in Westminster, London.

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In This Story: Novartis

Novartis International AG is a Swiss multinational pharmaceutical company based in Basel, Switzerland. It is one of the largest pharmaceutical companies by both market capitalization and sales.

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